TONETTO, ELENA
TONETTO, ELENA
Dipartimento di Scienze della vita e biotecnologie
A factor X variant with engineered activation peptide as innovative by-passing agent for haemophilia
file con accesso da definire2022 Tonetto, E.; Tarantino, R.; Testa, M. F.; Peretto, L.; Bernardi, F.; Pinotti, M.; Branchini, A.
An engineered factor X variant as a novel by-passing agent for hemophilia
file con accesso da definire2022 Tonetto, Elena; Testa, Maria Francesca; Tarantino, Rebecca; Peretto, Laura; Pinotti, Mirko; Branchini, Alessio
Base and Prime editing of DNA as a new therapeutic option for Hemophilia A
file con accesso da definire2022 Tonetto, Elena; Pignani, Silvia; Roman, Giacomo; Follenzi, Antonia; Bernardi, Francesco; Liu, David; Pinotti, Mirko; Balestra, Dario
Base and prime editing tools as correction approaches for rare genetic diseases
2025 Tonetto, Elena
Counteracting the Common Shwachman-Diamond Syndrome-Causing SBDS c.258+2T>C Mutation by RNA Therapeutics and Base/Prime Editing
2023 Peretto, Laura; Tonetto, Elena; Maestri, Iva; Bezzerri, Valentino; Valli, Roberto; Cipolli, Marco; Pinotti, Mirko; Balestra, Dario
Design of an engineered coagulation factor X as a novel by-passing agent for hemophilia
file con accesso da definire2023 Tarantino, Rebecca; Tonetto, Elena; Testa, Maria Francesca; Pinotti, Mirko; Branchini, Alessio
DNA base editing corrects common hemophilia A mutations and restores factor VIII expression in in vitro and ex vivo models
file con accesso da definire2024 Tonetto, Elena; Cucci, Alessia; Follenzi, Antonia; Bernardi, Francesco; Pinotti, Mirko; Balestra, Dario
New Genome Editing Approaches: Base And Prime Editing To Revert Hemophilia A-Causing Point Mutations
file con accesso da definire2022 Tonetto, E.; Pignani, S.; Roman, G.; Follenzi, A.; Bernardi, F.; Liu, D.; Pinotti, M.; Balestra, D.
| Titolo | Data di pubblicazione | Autore(i) | File |
|---|---|---|---|
| A factor X variant with engineered activation peptide as innovative by-passing agent for haemophilia | 2022 | Tonetto, E.; Tarantino, R.; Testa, M. F.; Peretto, L.; Bernardi, F.; Pinotti, M.; Branchini, A. | file con accesso da definire |
| An engineered factor X variant as a novel by-passing agent for hemophilia | 2022 | Tonetto, Elena; Testa, Maria Francesca; Tarantino, Rebecca; Peretto, Laura; Pinotti, Mirko; Branc...hini, Alessio | file con accesso da definire |
| Base and Prime editing of DNA as a new therapeutic option for Hemophilia A | 2022 | Tonetto, Elena; Pignani, Silvia; Roman, Giacomo; Follenzi, Antonia; Bernardi, Francesco; Liu, Dav...id; Pinotti, Mirko; Balestra, Dario | file con accesso da definire |
| Base and prime editing tools as correction approaches for rare genetic diseases | 2025 | Tonetto, Elena | |
| Counteracting the Common Shwachman-Diamond Syndrome-Causing SBDS c.258+2T>C Mutation by RNA Therapeutics and Base/Prime Editing | 2023 | Peretto, Laura; Tonetto, Elena; Maestri, Iva; Bezzerri, Valentino; Valli, Roberto; Cipolli, Marco...; Pinotti, Mirko; Balestra, Dario | |
| Design of an engineered coagulation factor X as a novel by-passing agent for hemophilia | 2023 | Tarantino, Rebecca; Tonetto, Elena; Testa, Maria Francesca; Pinotti, Mirko; Branchini, Alessio | file con accesso da definire |
| DNA base editing corrects common hemophilia A mutations and restores factor VIII expression in in vitro and ex vivo models | 2024 | Tonetto, Elena; Cucci, Alessia; Follenzi, Antonia; Bernardi, Francesco; Pinotti, Mirko; Balestra,... Dario | file con accesso da definire |
| New Genome Editing Approaches: Base And Prime Editing To Revert Hemophilia A-Causing Point Mutations | 2022 | Tonetto, E.; Pignani, S.; Roman, G.; Follenzi, A.; Bernardi, F.; Liu, D.; Pinotti, M.; Balestra, D. | file con accesso da definire |